Claris Bio Unveils Development Strategy and Planned Pivotal Study Supported by $118 Million Series B Financing
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Vera Received FDA Accelerated Approval for TRUTAKNA™ for Adult Patients with Primary IgA Nephropathy
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Incyte Completes Acquisition of Vega Therapeutics, a Wholly Owned Subsidiary of Star Therapeutics, Expanding its Hematology Portfolio
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City Therapeutics Announces $99.5 Million Series B Financing to Advance Next-Generation RNAi Therapeutics
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Incyte to Acquire Vega Therapeutics, a Wholly Owned Subsidiary of Star Therapeutics, Expanding its Hematology Portfolio into Bleeding Disorders
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Avenzo Therapeutics and Rallybio Corporation Announce Merger Agreement to Advance Next-Generation Oncology Therapies and $215 Million Concurrent Private Placement
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Baxfendy Approved in the US as the First and Only Aldosterone Synthase Inhibitor Treatment for Adults with Hypertension
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Seaport Therapeutics Announced Pricing of Upsized Initial Public Offering
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Coultreon Biopharma Raises $125 Million in Series A Financing to Advance Immunology Pipeline
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Avenzo Therapeutics to Present Updated Results from the Phase 1 Study of AVZO-021, a Potential Best-in-Class CDK2 Inhibitor, at the 2026 American Society of Clinical Oncology Annual Meeting
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Star Therapeutics Receives FDA Rare Pediatric Disease and Breakthrough Therapy Designations for VGA039 in Von Willebrand Disease Prophylaxis
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Seaport Announced Positive Proof of Concept Topline Results from Ongoing Phase 1 Trial of GlyphAgo™ in Healthy Volunteers
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Rapport and Tenacia Biotechnology Announced Strategic Collaboration for the Development and Commercialization of RAP-219 in Greater China
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VISEN Received China NMPA Approval for Once-Weekly Lonapegsomatropin for Pediatric Growth Hormone Deficiency
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BioAge Announced Pricing of Upsized $115 Million Public Offering
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Marea Unveils Positive Topline Phase 1 Data for MAR002 in Acromegaly; Demonstrates Potential for Best-in-Disease Efficacy and Dosing Profile
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BioAge Announced Positive Interim Phase 1 Data for BGE-102, a Novel Brain-Penetrant Inhibitor, Demonstrating Potential for Best-in-Class hsCRP Reduction in Participants with Elevated Cardiovascular Risk
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Vera Announced U.S. FDA Granted Priority Review to Biologics License Application for Atacicept for Treatment of Adults with IgA Nephropathy
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Aeovian Raised $55 Million to Advance First-in-Class Selective mTORC1 Inhibitor for Tuberous Sclerosis Complex-Related Epilepsy
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Vera Announced Positive ORIGIN Phase 3 Data for Atacicept in IgA Nephropathy
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Expedition Raised $165 Million in Oversubscribed Series A Financing to Advance Next-Generation DPP1 inhibitor for COPD
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Star Therapeutics Announced Oversubscribed $125 Million Series D Financing
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Avenzo Announced $60 Million Series B Financing
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ARTBIO Announced FDA Clearance of IND Application for Lead Alpha Radioligand Therapy AB001
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Rapport Announced Positive Topline Results from Phase 2a Clinical Trial of RAP-219 in Patients with Focal Onset Seizures
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Alkeus Announced Presentation of Positive Interim TEASE-3 Study Data in Early-Stage Stargardt Disease
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ARTBIO Announced $132 Million Series B Financing to Advance Pipeline of Alpha Radioligand Therapies and Expand Manufacturing and Supply Chain Infrastructure
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Quanta Announces Leadership Team Appointment and Highlights Clinical Program Progress
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Baxdrostat Met Primary and All Secondary Endpoints in BaxHTN Phase III Trial in Patients With Uncontrolled or Treatment Resistant Hypertension
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Marea Therapeutics Presents Preclinical Data on Novel Growth Hormone Receptor Antagonist Antibody, MAR002, for the Treatment of Acromegaly at ENDO 2025
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New 3-Year Phase 3 Data Confirmed Sustained Response to TransCon® PTH (Palopegteriparatide) Therapy in Adults with Hypoparathyroidism, Including Improvements in Biochemistries, Kidney Function, and Quality of Life
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Atsena Therapeutics Announces Alignment with FDA on Regulatory Pathway to Approval for ATSN-201 in X-Linked Retinoschisis (XLRS)
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AbbVie to Acquire Capstan Therapeutics, Further Strengthening Commitment to Transforming Patient Care in Immunology
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ArriVent Announced Positive Interim Firmonertinib Monotherapy Data From Global Phase 1b Study in EGFR PACC Mutant Non-Small Cell Lung Cancer and Plans to Advance into a Global Pivotal Study
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Vera Announced Atacicept Achieved 46% Proteinuria Reduction in ORIGIN Phase 3 Trial in Adults with IgA Nephropathy
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Avenzo Announced FDA Clearance of Investigational New Drug Application for AVZO-1418, a Potential Best-in-Class, Novel EGFR/HER3 Bispecific Antibody-Drug Conjugate
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Avenzo Announced FDA Clearance of Investigational New Drug Application for AVZO-023 (ARTS-023), a Potential Best-in-Class, Novel CDK4 Selective Inhibitor
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NorthSea Therapeutics Announces Publication of Positive Results from Phase 2b ICONA Clinical Trial of Icosabutate in Biopsy-Confirmed F1-F3 MASH in Journal of Hepatology
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Marea Therapeutics Presents Positive Data from Phase 2a Clinical Trial of MAR001, Being Developed for Cardiovascular Disease, in Late-Breaking Oral Session at the 93rd EAS Congress
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Atsena Therapeutics Granted U.S. FDA Regenerative Medicine Advanced Therapy Designation for ATSN-201 Gene Therapy to Treat X-linked Retinoschisis
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New 4-Year Data Shows Sustained Response to TransCon® PTH (Palopegteriparatide) Therapy in Adults with Hypoparathyroidism
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Alkeus Pharmaceuticals Presents Gildeuretinol Data During the Association for Research in Vision and Ophthalmology (ARVO) 2025 Annual Meeting May 4-8, 2025
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Aeovian Pharmaceuticals Doses First Participants in Phase 1 Clinical Trial, Strengthens Leadership Team and Raises Additional $50 Million Financing
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New Data Shows Improvements in Growth and Bone Morphometry in Children with Achondroplasia Treated with TransCon® CNP (Navepegritide)
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Marea Presented Positive Data from Phase 2a Clinical Trial of MAR001, Being Developed for Cardiovascular Disease, in Late-Breaking Oral Session at the 93rd EAS Congress
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Atsena Granted U.S. FDA Regenerative Medicine Advanced Therapy Designation for ATSN-201 Gene Therapy to Treat X-linked Retinoschisis
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Atsena Announced Oversubscribed $150 Million Series C Financing to Further Advance Ocular Gene Therapy Programs
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VISEN Pharmaceuticals Announced the Offer Price and Allotment Results of the Global Offering
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ArriVent BioPharma Enters Exclusive License with Lepu Biopharma for MRG007, an Antibody Drug Conjugate for the treatment of Gastrointestinal Cancers
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Natera Announces Successful Readout of Randomized, Phase III CALGB (Alliance) / SWOG 80702 Clinical Trial in Colorectal Cancer
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OnCusp Receives FDA Fast Track Designation for CUSP06 for the Treatment of Platinum-Resistant Ovarian Cancer
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Vera Therapeutics Acquires Global Rights to Novel, Next Generation Dual BAFF/APRIL Inhibitor
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Inozyme Pharma Announces Positive Interim Data for INZ-701 in Infants and Young Children with ENPP1 Deficiency and Key Program Updates
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Rapport Therapeutics Announces New Phase 1 Data, Supporting RAP-219’s Transformative Potential for CNS Disorders
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Marea Announces Topline Results from Phase 2a Clinical Trial of MAR001 for Cardiovascular Disease
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Quanta Announces IND Clearance by U.S. FDA for QTX3544, an Oral G12V-Preferring Multi-KRAS Inhibitor, and Other Pipeline Updates
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Exclusive: Avenzo picks up another ADC, this time with multi-partnered DualityBio
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Star Therapeutics Receives FDA Fast Track Designation for VGA039 in Von Willebrand Disease (VWD)
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BioAge Labs Announces Multi-Year Collaboration with Novartis to Discover Novel Targets for Therapies that Address Age-Related Diseases and Conditions
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Alkeus Receives FDA Rare Pediatric Disease and Fast Track Designations for Gildeuretinol as a Treatment for Stargardt Disease
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Axonis Announces $115M Series A Financing
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Vera Announces Pricing of Public Offering of Class A Common Stock
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Vera Announces 96-week eGFR Stabilization in ORIGIN Phase 2b Study of Atacicept in IgAN
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Seaport Closes $225M Oversubscribed Series B Financing Round
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Vera Announced Expanded Atacicept Development Program In Multiple Autoimmune Kidney Diseases
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Ascendis Presented New 3-Year Skeletal Dynamics Data for Adults with Hypoparathyroidism Treated with TransCon™ PTH (Palopegteriparatide) at ASBMR 2024
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BioAge Labs Announces Pricing of Upsized Initial Public Offering
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Ascendis Announced Topline Data From ApproaCH Trial of TransCon CNP
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ArriVent Announced Positive Proof-Of-Concept Global Phase 1b Interim Data for Firmonertinib Monotherapy In First-Line EGFR PACC Mutant Non-Small Cell Lung Cancer
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Ascendis Announced FDA has Approved YORVIPATH® (Palopegteriparatide) as the First and Only Treatment for Hypoparathyroidism in Adults
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BioAge Announces First Patient Dosed in the STRIDES Phase 2 Clinical Trial Evaluating Azelaprag as a Novel Treatment for Obesity in Combination with Tirzepatide
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Quanta Announces Dosing of First Patient in Phase 1/1b Clinical Trial of QTX3046 and Other Program Updates
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BioAge Labs Presents Preclinical Data for Apelin Receptor Agonist Azelaprag for Obesity Demonstrating Significant Improvements in Weight Loss and Body Composition When Combined with Incretin Drugs
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Marea Launches with $190M to Accelerate a New Generation of Medicines for Cardiometabolic Diseases
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Rapport Announces Pricing of Initial Public Offering
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ArriVent Announces a Multi-Target ADC Collaboration with Alphamab
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Vera Receives U.S. FDA Breakthrough Therapy Designation for Atacicept in Immunoglobulin A Nephropathy (IgAN)
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Ascendis Reports Significant and Sustained Improvements in Renal Function Reported for Adults with Chronic Hypoparathyroidism Treated with TransCon™ PTH
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Alkeus Announces Positive Interim Results Demonstrating No Signs of Disease Progression in Early-Stage Stargardt Disease Patients Treated with Gildeuretinol
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Seaport Launches with $100M Oversubscribed Series A Financing Round to Advance Novel Neuropsychiatric Medicines
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Inozyme Announces Positive Topline Data from Ongoing Phase 1/2 Trials of INZ-701 in Adults with ABCC6 Deficiency (PXE) and ENPP1 Deficiency
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Avenzo Therapeutics Announces $150M Oversubscribed Financing To Advance Emerging Oncology Pipeline
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Capstan Therapeutics Announces $175M Oversubscribed Series B Financing
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BioAge Announces $170M Oversubscribed Series D Financing to Accelerate Development of Obesity and Metabolic Disease Therapeutics
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Vera Announces Closing of Upsized Public Offering and Full Exercise of Underwriters’ Option to Purchase Additional Shares in Public Offering of Class A Common Stock
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Vera Announces Pricing of Upsized Public Offering of Class A Common Stock
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ArriVent Announces Pricing of Upsized Initial Public Offering
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Vera Announced Positive 72-Week Data Showing eGFR Stabilization in the Phase 2b ORIGIN Clinical Trial OLE in IgA Nephropathy
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Alkeus Presents Positive Interim Data Showing Gildeuretinol Halted Stargardt Disease Progression
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GSK Enters Agreement to Acquire Aiolos Bio
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OnCusp Therapeutics Raises Oversubscribed $100 Million Series A Financing to Advance Portfolio of Assets for Cancer Patients
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Bristol Myers Squibb Adds Premier Radiopharmaceutical Platform with Acquisition of RayzeBio
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Bristol Myers Squibb Strengthens Neuroscience Portfolio with Acquisition of Karuna Therapeutics
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Ascendis Announces Significant Health and Quality of Life Improvements Achieved in Children with Achondroplasia Treated for One Year with TransCon™ CNP (Navepegritide)
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Karuna Announces The Lancet Publication of Data from Phase 3 EMERGENT-2 Trial Evaluating KarXT in Schizophrenia
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Karuna Announces U.S. Food and Drug Administration Accepts New Drug Application for KarXT for the Treatment of Schizophrenia
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Aerovate Announces Simultaneous Completion of Enrollment in Phase 2b and Enrollment of First Patient into Phase 3 in IMPAHCT Trial for Pulmonary Arterial Hypertension
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Karuna Announces Positive Results from Phase 1b Ambulatory Blood Pressure Monitoring Trial of KarXT in Schizophrenia
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Karuna Announces Positive Results from Phase 1b Ambulatory Blood Pressure Monitoring Trial of KarXT in Schizophrenia
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Atsena Receives FDA Regenerative Medicine Advanced Therapy (RMAT) Designation for ATSN-101 Gene Therapy
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Vera Announced Positive Data from Phase 2b ORIGIN Study Showing Resolution of Hematuria in Majority of Patients
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Alkeus Presents Positive Gildeuretinol Trial Results Demonstrating Significant Slowing of Retinal Atrophic Lesions in Stargardt Disease
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ArriVent Receives FDA Breakthrough Therapy Designation for Furmonertinib: First-Line Treatment of Advanced or Metastatic Non-Small Cell Lung Cancer
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Aiolos Bio Launches with $245 Million Series A Investment to Advance Development of Novel, Phase 2-Ready TSLP Antibody
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FDA Selects RayzeBio to Participate in the Inaugural CDRP Program to Expedite Commercial Manufacturing Readiness for RYZ101 in GEP-NETs
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Karuna Submits New Drug Application to U.S. Food and Drug Administration for KarXT for the Treatment of Schizophrenia
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Bolt Receives Orphan Drug Designation for BDC-1001 for Treatment of Gastric Cancers
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RayzeBio Announces Pricing of Upsized $311 Million Initial Public Offering
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Natera Announces Pricing of $250 Million Follow-On Offering
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Star Therapeutics Raises $90 Million Financing to Accelerate its Pipeline of Novel Antibody Therapies
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Rapport Therapeutics Raises $150 Million in Series B Funding Round and Announces Key Board Appointments to Further Advance Precision Neuromedicine Platform
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Ikena Oncology Acquires Pionyr Immunotherapeutics in All-Stock Transaction
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Inozyme Announces Updates on Global Development Strategy of INZ-701 for the Treatment of ENPP1 Deficiency
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ArriVent Biopharma and InnoCare Pharma Announce Clinical Development Collaboration
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Vera Announces Positive Week 36 Efficacy and Safety Results of Phase 2b ORIGIN Clinical Trial of Atacicept in IgAN
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Ascendis Opens Compassionate Use Program for TransCon™ PTH (palopegteriparatide) in Germany
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Alkeus Announces $150 Million Series B Financing, Supporting Rapid Registration Path for gildeuretinol (ALK-001) in the Treatment of Stargardt Disease
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Ascendis Oncology Program Update Highlights Latest Clinical Data for Product Candidates
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RayzeBio Announces First Patient Dosed in Phase 3 ACTION-1 Study, Evaluating RYZ101 (Actinium-225 DOTATATE) in Neuroendocrine Tumors
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Y-mAbs’ DANYELZA® (naxitamab-gqgk) for the Treatment of High-Risk Neuroblastoma approved in Brazil
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Quanta Raises Over $50 Million in Series D Financing to Advance its Pipeline of KRAS Inhibitors
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Atsena Receives FDA Clearance of IND Application for ATSN-201, an Investigational Gene Therapy for the Treatment of X-linked Retinoschisis
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Antiva Biosciences Closes $53 Million Series E Equity Financing and Names Kristine Ball President and CEO
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Bolt Announces Positive Topline Data from BDC-1001 Phase 1 Dose-Escalation Trial in HER2-Expressing Tumors, Supporting Advancement to Phase 2 Clinical Studies
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ArriVent Biopharma Closes $155 Million Oversubscribed Series B Financing
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Karuna Announces Closing of Public Offering and Full Exercise of Option to Purchase Additional Shares
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Pionyr Immunotherapeutics and Gilead Change Exclusive Option Agreement
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Karuna Therapeutics Announces Positive Results from Phase 3 EMERGENT-3 Trial of KarXT in Schizophrenia
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RayzeBio Completes Phase 1b Enrollment in ACTION-1 Study, Evaluating RYZ101 (Actinium-225 DOTATATE) in Neuroendocrine Tumors
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Acquisition of CinCor Pharma by AstraZeneca Completed
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CinCor Pharma Announces Receipt of Minutes from End-of-Phase 2 Meeting with the U.S. Food and Drug Administration on Planned Phase 3 Program of Baxdrostat
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Atsena to Present Positive Interim Encore Data from the Phase I/II Clinical Trial of ATSN-101 for the Treatment of GUCY2D-associated Leber Congenital Amaurosis (LCA1)
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XyloCor Reports Positive Topline Safety and Efficacy Results from Phase 2 EXACT Clinical Trial of XC001 Novel Gene Therapy for Refractory Angina
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CinCor Pharma to be Acquired by AstraZeneca
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NorthSea Provides Clinical Update Reflecting Progress Across NASH and Metabolic Disorders Programmes
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RayzeBio Announces Issuance of Two Patents for RYZ101 (225Ac-DOTATATE)
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Vera Announces Positive Topline Results of Phase 2b ORIGIN Clinical Trial of Atacicept for the Treatment of IgA Nephropathy
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Lilly Completes Acquisition of Akouos Expanding Efforts to Help People with Genetic Diseases
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CinCor Pharma Announces Topline Data for Phase 2 HALO Trial Evaluating Selective Aldosterone Synthase Inhibitor Baxdrostat in Uncontrolled Hypertension
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Aerovate Publishes Results of Phase 1 Study Evaluating AV-101 for the Treatment of Pulmonary Arterial Hypertension in ERJ Open Research
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Ascendis Once-Weekly TransCon™ CNP Achieved Primary Efficacy Objective in Phase 2 ACcomplisH Trial of Children with Achondroplasia Aged 2 to 10 Years
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CinCor Announces Late-Breaking Presentation of Phase 2 BrigHtn Data on Baxdrostat in Treatment-Resistant Hypertension
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Vera Presents New Analysis of Phase 2a JANUS Trial of Atacicept in IgA Nephropathy and Positive Final Phase 2 Results of MAU868 in Kidney Transplant Recipients with Reactivated BK Virus Infection
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FDA Accepts for Priority Review Ascendis Pharma’s NDA for TransCon™ PTH in Adult Patients with Hypoparathyroidism
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Y-mAbs Announces Regulatory Filing for DANYELZA® (naxitamab-gqgk) in Brazil
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Lilly to Acquire Akouos to Discover and Develop Treatments for Hearing Loss
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Y-mAbs Announces Pivotal Data for Omburtamab
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RayzeBio Propels Forward with $418 Million Raised Since Inception to Advance Targeted Radiopharmaceuticals for Cancer
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Akouos Receives FDA Clearance of its IND Application for AK-OTOF, a Gene Therapy Intended for the Treatment of OTOF-mediated Hearing Loss
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CinCor Announces Closing of Upsized Public Offering and Full Exercise of Option to Purchase Additional Shares
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Karuna Announces Closing of Public Offering and Full Exercise of Option to Purchase Additional Shares
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Karuna Announces Positive Results from Phase 3 EMERGENT-2 Trial of KarXT in Schizophrenia
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CinCor Announces Positive Topline Data for Phase 2 BrigHtn Trial Evaluating Baxdrostat, its Selective Aldosterone Synthase Inhibitor, in Treatment-Resistant Hypertension
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Y-mAbs Announces Second Quarter Financial Results and Recent Corporate Developments
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CinCor Doses Last Patient in Phase 2 Study and Announce Initiation of Long-Term Extension Study for Baxdrostat in Uncontrolled Hypertension
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Inozyme Announces Positive Preliminary Data from Phase 1/2 Clinical Trial of INZ-701 in Subjects with ABCC6 Deficiency
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Y-mAbs’ Announces Clearance of IND for GD2-SADA
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Vera Completes Patient Enrollment in Phase 2b ORIGIN Clinical Trial of Atacicept for the Treatment of IgA Nephropathy
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Inozyme Announces Partnership with Rady Children’s Institute for Genomic Medicine to Advance Newborn Screening for Genetic Diseases
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Vera Reports Positive Interim Phase 2 Data Showing MAU868 Has Significant BK Antiviral Activity in Kidney Transplant Patients
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CinCor Doses First Patient in Phase 2 FigHTN-CKD Trial Evaluating the Selective Aldosterone Synthase Inhibitor Baxdrostat (CIN-107) in Patients with Uncontrolled Hypertension and Chronic Kidney Disease
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Regeneron has completed its acquisition of Checkmate Pharmaceuticals
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Pionyr Phase 1a Study of TREM2-targeting Antibody PY314 for the Treatment of Solid Tumors Featured at ASCO 2022
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Positive Results from VISEN’s Phase 3 Trial of Once-Weekly TransCon hGH in China Consistent with Ascendis Pharma’s Phase 3 Height Trial
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Inozyme Announces Positive Preliminary Data from Phase 1/2 Clinical Trial of INZ-701 in Patients with ENPP1 Deficiency
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Apellis Announces Closing of Public Offering of Common Stock and Full Exercise of Option to Purchase Additional Shares
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CinCor Pharma to be Added to Russell 2000® and Russell 3000® Indexes
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Apellis Announces Pegcetacoplan Showed Continuous and Clinically Meaningful Effects at Month 18 in Phase 3 DERBY and OAKS Studies for Geographic Atrophy (GA)
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Ascendis Announces Phase 3 PaTHway Trial of TransCon™ PTH in Adults with Hypoparathyroidism Met Primary and All Key Secondary Endpoints
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Pionyr Immunotherapeutics Doses First Patient in Phase 1b Expansion Study of PY314
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Natera and MinMinBear Foundation Announce Partnership to Provide Comfort and Support to Kidney Patients
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Gyroscope Therapeutics Acquisition is Complete
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Vera Therapeutics Announces Closing of Upsized Public Offering of Class A Common Stock and Full Exercise of Underwriters’ Option to Purchase Additional Shares
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Ascendis Receives European Approval for TransCon™ hGH for Pediatric Growth Hormone Deficiency
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CinCor Pharma Announces Pricing of Initial Public Offering
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Antiva Biosciences Named Winner of Global Women’s HealthTech Award by World Bank Group and Consumer Technology Association
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Novartis to Acquire Gyroscope Therapeutics for Up to $1.5 Billion
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NorthSea Therapeutics Completes $80 Million Series C Fundraising to Advance Clinical Programs in Metabolic Disorders
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ObsEva Announces Positive CHMP Opinion for Linzagolix, an Oral GnRH Antagonist, for the Treatment of Uterine Fibroids
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Vera Therapeutics Announces Acquisition of Monoclonal Antibody From Pfizer to Treat BK Virus in Transplant Patients
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Aerovate Therapeutics Announces Initiation of IMPAHCT Phase 2b/Phase 3 Trial of AV-101 In Pulmonary Arterial Hypertension
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NorthSea Announces Icosabutate Latest Phase 2b Interim Data Show Significant Decreases in NASH and Fibrosis Biomarkers Independent of Fibrosis Stage and Disease Severity
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Gyroscope Therapeutics Announces Sanofi Investment of up to $60 Million
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Antiva Biosciences Closes $31 Million Series D Equity Financing
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Quanta Therapeutics Announces Oversubscribed $60 Million Series C Financing to Advance Novel RAS-targeting Programs
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CinCor Pharma Raises $143 Million in Series B Financing
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NextCure Announces Publication of Preclinical Data for NC410
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Inozyme Pharma Announces Presentation of Data from ENPP1 Deficiency Development Program
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Gyroscope Therapeutics Announces Presentation of Positive Interim Phase I/II Data for Investigational Gene Therapy GT005
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NuCana Receives Fast Track Designation from the U.S. Food and Drug Administration for Acelarin® (NUC-1031) for the Treatment of Biliary Tract Cancer
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Y-mAbs Announces Priority Review of BLA for DANYELZA® (naxitamab-gqgk) in China
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Bolt Announces Clinical Collaboration with Bristol Myers Squibb to Study BDC-1001 in Combination with Opdivo®
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Ascendis Announces U.S. Food and Drug Administration Approval of SKYTROFA®, the First Once-weekly Treatment for Pediatric Growth Hormone Deficiency
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Akouos Announces European Commission Designation of AK-OTOF for the Treatment of Otoferlin Gene-Mediated Hearing Loss as an Orphan Drug
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ObsEva and Organon Enter Global License Agreement to Develop and Commercialize Ebopiprant (OBE022), an Investigational Agent Being Evaluated as a First-in-Class Treatment for Preterm Labor
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XyloCor Therapeutics Commences Phase 2 Component of Phase 1/2 EXACT Clinical Study of XC001 Gene Therapy for Refractory Angina
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Neurana Pharmaceuticals Announces Publication in Pain Management
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Athira Pharma Announces Initiation of Open Label Extension Study for LIFT-AD and ACT-AD Clinical Trials of ATH-1017 for Alzheimer’s Disease
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Y-mAbs Announces NMPA Submission of BLA for DANYELZA® (naxitamab-gqgk) in China
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Ascendis Announces Target Enrollment Achieved in the Phase 3 PaTHway Trial of TransCon™ PTH (palopegteriparatide) in Adults with Hypoparathyroidism (HP)
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Aerovate Therapeutics Announces Pricing of Upsized Initial Public Offering
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Y-mAbs’ 177Lu-omburtamab-DTPA for the Treatment of Patients with Medulloblastoma Receives Positive Opinion on Orphan Medicinal Product Designation by EMA
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Natera and BGI Genomics Announce Commercial Launch of the BGI/Natera Signatera Assay in China
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Karuna Therapeutics Announces Results from Phase 1b Trial Evaluating the Safety and Tolerability of KarXT in Healthy Elderly Volunteers
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Gyroscope Therapeutics Announces Research Collaboration Agreement with Children’s Medical Research Institute to Develop Novel Gene Therapy Capsids
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Pionyr and Abcam Extend Partnership to Evaluate TREM2-Expressing Cells in Cancer Patients
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Inozyme Announces Acceptance of First European Clinical Trial Application for Phase 1/2 Clinical Trial of INZ-701 in ABCC6 Deficiency
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Neurana Pharmaceuticals Announces 50% Enrollment in Phase 3, RESUME-1 Study
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VISEN Pharmaceuticals obtained IND approval for phase III China clinical trial (PaTHway China Trial) of TransCon PTH Solution for Injection (TransCon™ parathyroid hormone)
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Bolt Biotherapeutics and Genmab Announce Oncology Research and Development Collaboration
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Apellis Announces FDA Approval of EMPAVELI™ (pegcetacoplan) for Adults with Paroxysmal Nocturnal Hemoglobinuria (PNH)
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Vera Therapeutics Announces Pricing of Initial Public Offering
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Kiniksa Announces Positive Final Data from Phase 1 Trial of KPL-404
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Inozyme Pharma Publishes Data Supporting INZ-701 as a Potential Treatment for ENPP1 Deficiency
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Pfizer Acquires Amplyx Pharmaceuticals
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Galera Announces Updated Data from its Randomized, Multicenter, Placebo-Controlled Trial in Patients with Pancreatic Cancer
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Y-mAbs Submits Omburtamab Marketing Authorization Application to the European Medicines Agency
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Y-mAbs Provides Regulatory Update on Omburtamab
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Checkmate Pharmaceuticals Announces Initiation of Patient Dosing in Phase 2 Head and Neck Cancer Trial
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Gyroscope Therapeutics Files Registration Statement for Proposed Initial Public Offering in the United States
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Akouos Receives Orphan Drug and Rare Pediatric Disease Designations for AK-OTOF for the Treatment of Otoferlin Gene-Mediated Hearing Loss
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Kiniksa Announces Commercial Availability of ARCALYST ® (rilonacept) for Recurrent Pericarditis
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Natera and Tesis Labs Announce Strategic Collaboration on Prenatal Genetic Testing
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Amarin Receives European Commission (Ec) Approval for Vazkepa to Reduce Cardiovascular Risk
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VISEN’s TransConTM Human Growth Hormone Phase-III Clinical Trial in China Completes Target Patient Recruitment Number as Schedule
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Pionyr Immunotherapeutics Collaborates with Lonza to Support their Oncology Product Development
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Gyroscope Therapeutics Announces $148 Million Raised in Series C Financing
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XyloCor Therapeutics Completes Oversubscribed $41.9 Million Series A Financing To Advance Novel Gene Therapy Pipeline For Coronary Artery Disease
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Kiniksa Announces FDA Approval of ARCALYST ® (rilonacept) for Recurrent Pericarditis
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The Balancing Act® on Lifetime to Feature ENPP1 Deficiency
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Coherus BLA Filing for Adalimumab Biosimilar Candidate Accepted by FDA for Review
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ObsEva Provides Business Outlook for 2021
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Bolt Biotherapeutics Prices Upsized Initial Public Offering
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Athira Pharma Announces Pricing of Public Offering of Common Stock
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Vera Therapeutics Launches with $80 Million Series C Financing to Develop Phase 2b Novel Biologic for Kidney Disease
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Akouos and Blueprint Genetics Announce the Resonate Program to Improve Access to Genetic Testing for Individuals with Auditory Neuropathy
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VISEN Closes $150 Million Series B Financing to Accelerate the Development & Commercialization of its Innovative Endocrinology Therapies in Greater China
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Positive Phase 2b ICONA interim Results for Icosabutate in NASH Patients
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Merus Granted FDA Fast Track Designation of Zenocutuzumab for the Treatment of Patients with Neuregulin 1 Fusion Cancers
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Inozyme Pharma Announces Authorization to Proceed in U.S. and U.K. with Phase 1/2 Clinical Trial of INZ-701 for the Treatment of ENPP1 Deficiency
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Ascendis Pharma A/S Announces Filing of Investigational New Drug Application to Initiate TransCon™ TLR7/8 Agonist Clinical Program
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Neurana Pharmaceuticals Announces First Patient Enrolled in Phase 3, RESUME-1 Study
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Y-mAbs Signs Distribution Agreement with Swixx for DANYELZA® (naxitamab-gqgk) and Omburtamab in Eastern Europe
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Y-mAbs Signs License Agreement with SciClone for DANYELZA® (naxitamab-gqgk) and Omburtamab in China
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Merus and Sema4 Enter Into an Agreement to Support Merus’ Phase 1/2 Clinical Trial of Zenocutuzumab
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Atsena Therapeutics Raises $55 Million Series A Financing to Advance LCA1 Gene Therapy Clinical Program
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ObsEva Announces Additional Phase 3 PRIMROSE 1 and 2 Study Results Confirming Sustained Efficacy and Continued Safety of linzagolix in the Treatment of Uterine Fibroids
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Neurana Pharmaceuticals Announces Top-Line Results from Tolperisone Phase 1 CNS Effects Study
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Athira Pharma Awarded $15 Million Grant from National Institute on Aging to Support ACT-AD Clinical Trial in Alzheimer’s Disease
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Checkmate Pharmaceuticals Announces Clinical Collaboration with Bristol Myers Squibb to Evaluate CMP-001 in Combination with Nivolumab
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Natera Announced Second Largest Commercial Insurer Covers Non-Invasive Prenatal Testing for All Pregnancies
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Athira Pharma Announces Initiation of Patient Dosing for Treatment of Mild-to-Moderate Alzheimer’s Disease
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FDA Approves Y-mAbs’ DANYELZA® (naxitamab-gqgk) for the Treatment of Neuroblastoma
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Neurana Pharmaceuticals Announces Publication in the Journal of Pain Research
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Amarin Shares Topline Data from Partner’s Pivotal Phase 3 Study of Vascepa® (Icosapent Ethyl) in Mainland China
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Pionyr Immunotherapeutics Initiates Phase 1 Clinical Study of PY314
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Chiasma Announces Positive Topline Results from the MPOWERED™ Phase 3 Clinical Trial
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ObsEva SA Reports Positive Topline Results of the PROLONG Proof-of-Concept Trial of Ebopiprant (OBE022) for Treatment of Preterm Labor
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Kiniksa Announces Breakthrough Therapy Designation Granted to Vixarelimab for the Treatment of Pruritus Associated with Prurigo Nodularis
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Merck to Acquire VelosBio
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Ascendis Pharma A/S Receives Orphan Designation for TransCon™ PTH for Treatment of Hypoparathyroidism in Europe
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VelosBio Announces First Patient Dosed in Phase 2 Trial of VLS-101 in Solid Tumors
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Y-mAbs’ Nivatrotamab for the Treatment of Patients with Neuroblastoma Granted Orphan Drug Designation & Rare Pediatric Disease Designation by FDA
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Kiniksa Announces Positive Data from Phase 2 Trial of Mavrilimumab in Giant Cell Arteritis
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Sanofi Completes Principia Biopharma Inc. Acquisition
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Athira Pharma Announces Pricing of Initial Public Offering
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Principia Announces First Patient Dosed in Phase 2A Trial of Rilzabrutinib in IgG4-Related Disease
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Galera Therapeutics Announces Dosing of First Patient in a Randomized, Double-Blind Pilot Phase 2 Clinical Trial of GC4419 for COVID-19
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Kiniksa Announces U.S. Orphan Drug Designation for Mavrilimumab for the Treatment of Giant Cell Arteritis
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Natera Launches Initiative to Transform the Management of Cancer Patients in Organ Transplantation
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Ascendis Pharma Submits Marketing Authorisation Application to the European Medicines Agency for TransCon™ hGH
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Sanofi to Acquire Principia Biopharma
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Ascendis Pharma Receives Orphan Designation for TransCon™ CNP for the Treatment of Achondroplasia in Europe
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Aerovate Therapeutics Emerges With $72.6 Million Funding for Potential Disease-Modifying Pulmonary Arterial Hypertension Therapy
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Inozyme Pharma Announces Closing of Initial Public Offering and Full Exercise by Underwriters of Option to Purchase Additional Shares
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Karuna Therapeutics and PsychoGenics Announce Drug Discovery Collaboration
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Chiasma Announces 48-Week Safety and Efficacy Data from the Open-Label Extension Study of its CHIASMA OPTIMAL Phase 3 Trial Evaluating MYCAPSSA®
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Checkmate Granted FDA Fast Track Designation for CMP-001 Combined with PD-1 Blockade
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Merus announces FDA Orphan Drug Designation of Zenocutuzumab for the Treatment of Pancreatic Cancer
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Inozyme Pharma Announces Pricing of Initial Public Offering
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Kiniksa Pharmaceuticals, Ltd. Announces Pricing of Upsized Public Offering
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Amplyx Announces Positive Top-Line Data in Phase 2 Clinical Trial Of Novel Antifungal Fosmanogepix
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Checkmate Pharmaceuticals Executes a Snappy 1-2 Biotech Gambit — Big Crossover Followed by an Instant IPO
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Inozyme Pharma Acquires ENPP1 Deficiency Program Assets from Alexion Pharmaceuticals
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Kiniksa Announces U.S. Orphan Drug Designation for Rilonacept for the Treatment of Pericarditis
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Natera Recognized as a ‘Force for Change’ by Leading Women Entrepreneurs (LWE)
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VelosBio Raises $137 Million in Series B Financing to Advance Development of ROR1-Directed Therapeutics in Oncology
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NextCure Initiates Phase 1/2 Clinical Study of NC410, a Novel Immunomedicine, for Solid Tumors
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Ascendis Pharma A/S Receives Positive Opinion from the Paediatric Committee of the European Medicines Agency on the Agreement of a Paediatric Investigation Plan
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ObsEva Announces Positive Results from two Phase 3 Studies, PRIMROSE 1 and 2, of Yselty® (linzagolix) for the Treatment of Uterine Fibroids
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Y-mAbs Announces Initiation of Submission of Omburtamab Rolling Biologics License Application to the FDA
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Kiniksa Announces Positive Data from Phase 3 Trial of Rilonacept in Recurrent Pericarditis (RHAPSODY
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Chiasma Announces FDA Approval of MYCAPSSA® (Octreotide) Capsules, the First and Only Oral Somatostatin Analog
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Ascendis Pharma A/S Announces Submission of Biologics License Application (BLA) to FDA for TransCon™ hGH in Pediatric Growth Hormone Deficiency
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Akouos Announces Pricing of Initial Public Offering
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Karuna Therapeutics Announces Positive End-of-Phase 2 Meeting with the FDA for KarXT for the Treatment of Acute Psychosis in Patients with Schizophrenia
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Gilead Sciences Secures Exclusive Option to Acquire Pionyr Immunotherapeutics
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Vascepa® Shows Significant Cardiovascular Risk Reduction in People with Diabetes in Prespecified & Post Hoc Subgroup Analyses
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Principia Announces Positive Data from its Phase 2 Part B Trial in Pemphigus
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Checkmate Pharmaceuticals Secures $85 Million in Series C Financing
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Athira Pharma Closes $85 Million Series B Financing
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Vascepa® Shows Significant Reduction in Coronary Revascularization in Prespecified Tertiary Endpoint Analyses
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Inozyme Pharma & GACI Global Initiate Patient Study to Improve Understanding of the Impact of Disease in Patients with ENPP1 Deficiency & ABCC6 Deficiency
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Kiniksa Pharmaceuticals, Ltd. Announces Pricing of Public Offering
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Galera Therapeutics Announces New Data from the Phase 2b Trial on the Effect of Avasopasem Manganese on Cisplatin-Induced Chronic Kidney Disease
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AFYX Therapeutics Achieves Primary Endpoint in Phase 2b Trial of Rivelin-CLO in Patients with Oral Lichen Planus
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Kiniksa Announces Phase 2 Clinical Trial of Vixarelimab (KPL-716) in Prurigo Nodularis Meets Primary Efficacy Endpoint
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Ascendis Pharma A/S Announces Top-line Data from Fixed Dose Portion of Phase 2 Trial
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Natera Prices $250 Million Convertible Senior Notes Due 2027
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Coherus BioSciences Prices $200.0 Million Convertible Senior Subordinated Notes Offering
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Ascendis Pharma A/S Receives Orphan Drug Designation for TransCon™ hGH as Treatment for Growth Hormone Deficiency in the United States
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Y-mAbs Announces Submission of Naxitamab Biologics License Application to U.S. FDA
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Akouos Closes $105 Million Series B Financing
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Y-mAbs Announces Positive Pre-BLA Meeting with FDA for Omburtamab
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Promedior Announces Completion of Acquisition by Roche
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Astellas Completes Acquisition of Audentes Therapeutics
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Chiasma Announces FDA Acceptance Of MYCAPSSA® New Drug Application Resubmission
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NorthSea Therapeutics Announces US $40 Million Series B Financing to Complete Phase IIb ICONA study in NASH
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Astellas Enters into Definitive Agreement to Acquire Audentes Therapeutic
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Karuna Therapeutics Announces Pricing of $250 Million Public Offering of Common Stock
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Karuna Therapeutics Announces KarXT Met Primary Endpoint in Phase 2 Clinical Trial of Acute Psychosis in Patients with Schizophrenia
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Promedior Enters Into Definitive Merger Agreement To Be Acquired By Roche
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Spark Therapeutics Wins Prix Galien USA Award for LUXTURNA® (voretigene neparvovec-rzyl) as Best Biotechnology Product
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Ascendis Pharma A/S Receives Orphan Designation for TransCon™ hGH for the Treatment of Pediatric Growth Hormone Deficiency in Europe
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Aeovian Pharmaceuticals Raises $37 Million Series A Financing to Advance Selective mTORC1 Inhibitors into the Clinic for Rare and Age-Related Diseases
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Marinus Pharmaceuticals Announces Positive Top-Line Results With Ganaxolone in Phase 2 Refractory Status Epilepticus Trial
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Neurana Pharmaceuticals Announces Positive Topline Results from Phase 2 STAR Study of Tolperisone in Acute Muscle Spasms of the Back
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Akouos Discloses Lead Program, AK-OTOF, a Potential Gene Therapy for Sensorineural Hearing Loss
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Natera Publishes Largest NIPT Outcomes Study Demonstrating Robust Clinical Performance Over a 4-year Period
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ObsEva SA Announces $75 Million Credit Facility with Oxford Finance LLC
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Alimera Announces ILUVIEN® Regulatory Approval in Australia for the Treatment of Diabetic Macular Edema
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Natera Publication Demonstrates Unique Ability of Panorama Test to Determine Zygosity in Twin Pregnancies
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Chiasma Announces Positive Phase 3 Top-Line Results From CHIASMA OPTIMAL Clinical Trial Of Mycapssa®
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Synlogic Reports Positive Top-line Data from Phase 1/2a Study of SYNB1618 in Patients with Phenylketonuria
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ObsEva SA Announces Completion of Patient Recruitment in PRIMROSE 1
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Karuna Therapeutics Announces Pricing of Upsized Initial Public Offering
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CinCor Pharma Closes $50 Million Series A
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Inozyme Pharma Raises $67 Million in Series A2 Financing
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Amarin shares new updates to the American Diabetes Association 2019 Standards of Medical Care in Diabetes
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Iterum Therapeutics Receives QIDP for Oral and IV Sulopenem in Four Additional Indications as well as Fast Track Designation
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Ascendis Pharma Announces Once-weekly TransCon™ Growth Hormone Demonstrated Superiority on Primary Endpoint
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Spark Therapeutics Enters into Definitive Merger Agreement with Roche
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Kiniksa Pharmaceuticals Announces Pricing of Public Offering
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XyloCor Therapeutics Raises $17 Million in Series A
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BioClin Therapeutics Announces Name Change to Rainier Therapeutics
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NextCure Completes a $93M Series B Financing
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InCarda Completes $42M Oversubscribed Series B Financing
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NextCure and Lilly Announce Collaboration to Discover and Develop Novel Immuno-Oncology Medicines
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U.S. FDA Approves Coherus Biosciences’ UDENYCA™
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ObsEva Reports Additional Positive Phase 3 Results IMPLANT 2 Trial Following IVF
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ObsEva’s Final Results of Phase 2b EDELWEISS Trial Shows Sustained Efficacy and Safety
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Entasis Therapeutics Announces Pricing of Initial Public Offering
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Coherus Biosciences Receives European Commission Approval for Udenyca™
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Amarin’s REDUCE-IT™ Cardiovascular Outcomes Study of Vascepa® Capsules Met Primary Endpoint
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Y-mAbs Therapeutics Announces Pricing of Initial Public Offering
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Galera Therapeutics Raises $150M
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BioClin Therapeutics Announces New Leadership
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Principia Biopharma Announces Pricing of Initial Public Offering
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A women’s health startup tried to drum up interest for a much-needed drug. Many men didn’t get it.
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Akouos Raises $50M Series A Financing
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Iterum Announces the Pricing of Initial Public Offering
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Kiniksa Pharmaceuticals, Ltd. Announces Pricing of Initial Public Offering
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Entasis Therapeutics Initiates Clinical Studies of the Oral Extended-Spectrum Beta-Lactamase Inhibitor ETX0282
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BioClin Therapeutics, Inc., Completes $50M Series B Financing with Addition of New Investors
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Edge Therapeutics Provides Update following Interim Analysis of Phase 3 NEWTON 2 Study
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Medeor Therapeutics Awarded $18.8M From the California Institute for Regenerative Medicine
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Audentes Announces Positive Interim Data from First Dose Cohort of ASPIRO
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Ascendis Announces Completion of Target Enrollment in Phase 3 Trial of TransCon Growth Hormone
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Spark Therapeutics Announces FDA approval of LUXTURNA™
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Aerie Pharmaceuticals Announces U.S. FDA Approval of Rhopressa®
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Aclaris Therapeutics Receives FDA Approval for the Treatment of Raised Seborrheic Keratoses
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Pionyr Immunotherapeutics Completes $62M Series B Financing
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Y-mAbs Announces Closing of $30M Extension of Private Equity Placement
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Medeor Therapeutics Raises $57M In Series B Financing
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Apellis Announces the Pricing of Initial Public Offering
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ObsEva Announces Completion of Patient Recruitment for the Treatment of Endometriosis
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NuCana PLC Announces Pricing of Initial Public Offering
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Entasis Announces $31.9M Extension of Series B Financing
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Apellis Pharmaceuticals Announces $60M Series E Financing
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Amplyx Pharmaceuticals Raises $67M in Series C Financing
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Art Krieg comes down from the mountain with a $27M round for Checkmate Pharmaceuticals
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Virtual biotech Antiva sets out on a big R&D quest, armed with a $22M round for an HPV therapy
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Atsena Announces Positive 12-month Safety and Efficacy Data from Ongoing Phase I/II Clinical Trial of ATSN-101
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